

Presentaciones


Anne Pariser, MD - An Introduction To Preclinical Therapeutics Development
Adam L. Hartman, MD, FAAP, FAAN, FANA, FAES - Clinical Trials 101
Steven L. Roberds, PhD - The Power of Community: Clinical Trial Experience in Tuberous Sclerosis Complex
Herramientas y recursos


ClinicalTrials.gov - Find out if there are or have been any Clinical Trials for your disorder or related co-morbidities
NCATSToolkit for Patient-focused Therapeutics Development
RaDaR - Rare Diseases Registry Program
Artículos


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